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For those of you who have been following our journey towards gene therapy for GNE myopathy, here’s a detailed conversation with our board chair Ralph Loren talking shop with our CEO Lalé Welsh.
About NDF: Our mission is to enhance the quality of the lives of people living with GNE Myopathy through advocacy, education, outreach, and funding critical research focused on treatments and a cure.
To learn more about GNE Myopathy visit: https://www.CureGNEM.org
By Neuromuscular Disease FoundationFor those of you who have been following our journey towards gene therapy for GNE myopathy, here’s a detailed conversation with our board chair Ralph Loren talking shop with our CEO Lalé Welsh.
About NDF: Our mission is to enhance the quality of the lives of people living with GNE Myopathy through advocacy, education, outreach, and funding critical research focused on treatments and a cure.
To learn more about GNE Myopathy visit: https://www.CureGNEM.org