This episode offers an overview of cutting-edge biotechnologies and gene therapies revolutionizing treatment options. It provides a narrative on breakthrough therapies, mechanisms, and regulatory challenges with real-world data. It further explores the origin of ideas that lead to amazing therapies, target selection, preclinical evaluation, and toxicology studies in animals.

The conversation analyzes the FDA and the steps involved in pharmaceutical development. Discussing clinical trials, it explores all of the phases, the need for accurate data, and what happens when phase three trials fail. The conversation takes a turn by examining examples of driving new therapies and what mechanisms are leading these developments.