Tommy and Linda Pham turned their heartbreak over their son Raiden's ultra-rare disease diagnosis, UBA5 disorder, into hope for others. There are only 30 known cases in the world, but the Phams' relentless determination and their partnership with UMass Chan Medical School could pave the way for gene therapy advancements.

🎧 Listen and subscribe to all episodes of Rare Diseases, Real Stories: umassmed.edu/rarediseasesrealstories

💜 To learn more about the Raiden Science Foundation, visit the foundation's website at: https://www.raidenscience.org/. Follow Raiden's journey on Instagram: @raiden_journey.

💜 UBA5 disorder resources and support

Raiden Science Foundation

Translational Institute for Molecular Therapeutics at UMass Chan Medical School

🔗 Share Raiden's story using the following hashtags: #RareDiseasesRealStories, #RareDiseases, #podcast

Interested in learning more about gene therapy research? Email us at: [email protected]