Rare and Orphan Diseases

Host: Jennifer Caudle, DO

Guest: Leonard A Valentino, MD

Unfortunately, recognizing and diagnosing patients with bleeding disorders is only the first of many challenges. Once a diagnosis is reached, patients may face a variety of chronic health challenges and even altered family dynamics. Fortunately, recent treatments and developments—and even those on the horizon—can help alleviate the burden of bleeding disorders on patients and their loved ones. Join Dr. Jennifer Caudle as she uncovers those important efforts with Dr. Leonard Valentino, President and Chief Executive Officer at the National Hemophilia Foundation.

Host: Charles Turck, PharmD, BCPS, BCCCP

Guest: Joshua Richter, MD

Here to share his perspective on the use of triplet therapy for the treatment of multiple myeloma is Dr. Joshua Richter. Dr. Richter shares a patient case and speaks with Dr. Charles Turck about why this treatment may be an option for some patients.

Host: Charles Turck, PharmD, BCPS, BCCCP

Guest: Emily Carroll, JD, MSW

The No Surprises Act aims to protect consumers from surprise medical bills. But how exactly does it go about doing that, and what’s the current status of its implementation? Joining Dr. Charles Turck to share progress and challenges associated with the No Surprises Act is Ms. Emily Carroll, a senior legislative attorney for the American Medical Association's Advocacy Resource Center.

Guest: Arlene B. Chapman, MD

Guest: Michel Chonchol, MD

This Expert Exchange webcast aims to improve clinicians’ awareness of emerging agents in the treatment of patients with ADPKD.

Host: Jennifer Caudle, DO

Guest: Mikkael A. Sekeres, MD, MS

Guest: Sara M. Tinsley, PhD, ARNP, AOCNP

Please note: This activity is no longer available for continuing education credit.

There is a lack of available therapeutic options for the management of patients with myeloid malignancies, including myelodysplastic syndromes (MDS), chronic myelomonocytic leukemia (CMML), and acute myeloid leukemia (AML). Novel therapeutic approaches are being evaluated, particularly those that target the NEDD8-activating enzyme (NAE). Evaluating the rationale for NAE inhibition, assessing emerging safety and efficacy data on use of NAE inhibitors in myeloid malignancies, and developing strategies based on the evolving implications of this research will allow for greater understanding of their potential impact on management and health outcomes of patients with MDS, CMML, and AML.

Guest: Michel Chonchol, MD

Guest: Frederic Rahbari-Oskoui, MD, MSc

This Expert Exchange webcast aims to improve clinicians’ ability to manage patients diagnosed with ADPKD.

Guest: Matthew B. Lanktree, MD, PhD

Guest: Neera Dahl, MD, PhD

This Expert Exchange webcast aims to improve clinicians’ ability to properly monitor disease progression and make treatment decisions based on prognostic indicators.

Guest: Arlene B. Chapman, MD

Guest: Matthew B. Lanktree, MD, PhD

This Expert Exchange webcast aims to improve clinicians’ ability to detect and diagnose ADPKD in at-risk patients.

Guest: Jimmy T. Lee, MD

Guest: Arlene B. Chapman, MD

This Expert Exchange webcast aims to better define the importance radiological imaging plays in the management of patients with autosomal dominant polycystic kidney disease (ADPKD).

Guest: Lauren K. Brooks, MD

During this unprecedented time, finding the best approach to providing treatment for patients with thyroid cancer can be a challenge. Endocrinologist Dr. Lauren Brooks of Penn Medicine Lancaster General Health shares some of her approaches to this dilemma and stresses the importance of keeping up on routine practices during the COVID-19 pandemic.

Published September 28, 2020