Larry Luxner, senior correspondent for Rare Disease Advisor, interviews Dr. Abby Sandler of the National Cancer Institute.

Larry Luxner, senior correspondent for Rare Disease Advisor, interviews Yale University hematologist George Goshua, MD, who has completed a cost analysis of gene therapy versus standard of care in patients with sickle cell disease.

Larry Luxner, senior correspondent for Rare Disease Advisor, interviews Arushi Khurana, MBBS, a hematologist and lead author of a study showing that minorities are less likely to receive front-line therapy for diffuse large B-cell lymphoma than white patients.

Larry Luxner, senior correspondent for Rare Disease Advisor, interviews Catherine Broome, MD, on the relative benefits to quality of life by treating immune thrombocytopenia patients with efgartigimod.

Larry Luxner, senior correspondent for Rare Disease Advisor, interviews Paul W. Noble, MD, director of the Women’s Guild Lung Insitute at Cedars-Sinai Medical Center in Los Angeles, about his work exploring zinc as a potential therapy for idiopathic pulmonary fibrosis.

Larry Luxner, senior correspondent for Rare Disease Advisor, interviews Federico Stella, MD, on the controversial practice of severely restricting the diets of patients who have just undergone stem cell transplants.

Larry Luxner, senior correspondent for Rare Disease Advisor, interviews Abigail Jenkins, president and CEO of Gamida Cell Ltd., on the company's development of omidubicel as an alternative to umbilical cord blood in stem cell transplants for myelofibrosis and other patients.

Larry Luxner, senior correspondent for Rare Disease Advisor, interviews Peter Saltonstall, president and CEO of the National Organization for Rare Disorders (NORD), on the 40th anniversary of the landmark Orphan Drug Act.

Larry Luxner, senior correspondent for Rare Disease Advisor, interviews Sara Rothschild, the new executive director of the Life Raft Group, the nation's chief nonprofit advocating on behalf of patients with gastrointestinal stromal tumor (GIST).

Larry Luxner, senior correspondent for Rare Disease Advisor, interviews Philip J. Brooks, PhD, acting director of the Division of Rare Diseases Research Innovation at NCATS. Dr. Brooks describes the mission of the Bespoke Gene Therapy Consortium, which recently marked its first anniversary.