Gene therapy, hemostatic rebalancing therapies, memetic therapies, and even factor replacement therapy are all currently being explored in clinical trials, but while these therapies are paving the way to historical treatment ease and efficacy, they are also sweeping the hemophilia community into uncharted territory of potentially new challenges that must be addressed. This episode explores the current state of novel therapy investigation in hemophilia.

Contributors:

Dr. Maria Elisa Mancuso

Dr. Glenn Pierce

Dr. Steven Pipe

Dr. Lindsey George

Dr. Margareth Ozelo

Dr. Guy Young

Dr. Michael Recht

Dr. Rich Gorman

Mark Skinner

Luke Pembroke

 

Senior Advisor:

Dr. Donna DiMichele

Links to learn more:

• Future Therapies - National Hemophilia Foundation
• 2021 clinical trials update: Innovations in hemophilia therapy
• Advances in the management of haemophilia: emerging treatments and their mechanisms
• Emerging drugs for hemophilia A: insights into phase II and III clinical trials
• Discussing investigational AAV gene therapy with hemophilia patients: A guide
• Hemophilia Clinical Trials - ClinicalTrials.gov

Show Notes:

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