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Annemieke Aartsma-Rus and Elizabeth Vroom discuss with Patricia Lobo the developments in Duchenne muscular dystrophy therapy and how this can serve as a paradigm for development of treatment for rare diseases.
Annemieke Aartsma-Rus and Elizabeth Vroom discuss with Patricia Lobo the developments in Duchenne muscular dystrophy therapy and how this can serve as a paradigm for development of treatment for rare diseases.
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